It targets familial diseases that include Alzheimer's, Parkinson's and Huntington's disease.

Source: https://seekingalpha.com/article/4635634-week-in-review-hasten-signs-325-million-deal-for-china-rights-to-pcsk9-cholesterol-therapy?source=feed_all_articles

This drug is being evaluated in multiple studies of patients with Huntington's disease, a fatal condition with no cure that affects movement, cognition, and mental health.

Source: https://seekingalpha.com/article/4614654-sage-therapeutics-zuranolone-august-approval-likely-opportunity-uncertain?source=feed_all_articles

Very occasionally, it's possible to develop Huntington's disease without having a history of it in your family.

Source: https://www.dailymail.co.uk/news/article-11643031/Brilliant-Stanford-geneticist-87-ordered-pay-29m-friend-invested-fake-miracle-cure.html?ns_mchannel=rss&ns_campaign=1490&ito=1490